Cardiomyopathy
Basics
- Myocardial diseases causing structural and functional heart abnormalities without coronary artery disease, congenital defects, valvular disease, or hypertension sufficient to explain dysfunction.
- Cause 5-10% of heart failure cases.
Classification
- Primary (mainly cardiac):
- Genetic: Hypertrophic cardiomyopathy (HCM), Arrhythmogenic RV cardiomyopathy/dysplasia (ARVC/D), LV noncompaction (LVNC), glycogen storage diseases, conduction defects, mitochondrial myopathies, ion channel disorders (LQTS, Brugada, CPVT).
- Mixed: Dilated cardiomyopathy (DCM), restrictive cardiomyopathy (RCM).
- Acquired: myocarditis, stress cardiomyopathy, peripartum, tachycardia-induced, infants of diabetic mothers.
- Secondary: ischemic, valvular, hypertensive, congenital heart disease.
Epidemiology
- DCM incidence: 5-8 per 100,000 annually; prevalence ~1:2500; most common heart transplant indication.
- HCM prevalence: ~1:500 adults; 50% familial.
Etiology and Pathophysiology
- HCM: LV hypertrophy (>15 mm), nondilated, disproportionate to hemodynamic stress.
- ARVC/D: RV progressive myocyte loss with fatty/fibrofatty replacement, possible myocarditis association.
- LVNC: Congenital "spongy" LV myocardium.
- LQTS: Ion channelopathy with prolonged ventricular repolarization.
- DCM: Ventricular dilation, systolic dysfunction, often genetic, infectious, toxic causes.
- RCM: Normal/reduced ventricular volume with restrictive filling and biatrial enlargement.
- Myocarditis: Inflammation from toxins, drugs, infections.
- PPCM: DCM variant with LV systolic dysfunction and heart failure of unknown etiology.
- Stress cardiomyopathy: Acute reversible LV dysfunction after psychological stress.
- Endocrine, nutritional, autoimmune, infectious, infiltrative, storage, neuromuscular, toxic, and idiopathic causes also contribute.
Risk Factors
- Same as etiology (genetic predisposition, toxins, infections, systemic diseases).
Diagnosis
History
- Dyspnea, orthopnea, PND, chest pain, edema, abdominal bloating/pain.
Physical Exam
- Tachypnea, Cheyne-Stokes respiration, low pulse pressure, cool extremities, JVD, bibasilar rales, tachycardia, displaced PMI, S3 gallop, systolic murmur, hepatosplenomegaly, ascites, peripheral edema.
Differential Diagnosis
- Severe pulmonary disease, primary pulmonary hypertension, recurrent PE, constrictive pericarditis, advanced malignancy, anemia.
Diagnostic Tests
- ECG: LV hypertrophy, conduction delay, atrial fibrillation, old infarcts.
- Chest X-ray: cardiomegaly, increased upper lobe vasculature, pleural effusions.
- Echocardiogram:
- DCM: four-chamber enlargement, global hypokinesis, mural thrombi.
- HCM: severe LV hypertrophy, systolic anterior motion of mitral valve, mitral regurgitation, dynamic obstruction.
- RCM: low voltage ECG, pseudoinfarction pattern.
- Cardiac MRI: characterizes myocarditis, infiltrative diseases; patchy delayed enhancement in HCM.
- Stress myocardial perfusion imaging: rule out ischemia.
- Cardiac catheterization: exclude ischemic heart disease.
- Genetic testing and counseling.
Treatment
Medications
- Treat heart failure per guidelines.
- Avoid preload reduction (diuretics) and digoxin in obstructive HCM as they may worsen obstruction.
- Negative ionotropes/chronotropes: Ξ²-blockers, calcium channel blockers.
- ICD for prevention of VT/VF/sudden cardiac death; especially with family history of SCD.
- Anticoagulation and rate control for atrial fibrillation.
- Immunosuppression for myocarditis-related DCM.
- Tafamidis for transthyretin amyloid-related RCM.
Referral
- Heart failure team management.
- Early transplant evaluation if refractory.
Ongoing Care
- Dietary salt and fluid restriction, low-fat diet.
- Regular follow-up for symptoms and management adherence.
Prognosis
- NYHA Class IV: 20-40% mortality within 1 year without transplant.
- With transplant: 1-year survival up to 94%.
Complications
- Progressive heart failure, syncope, renal failure, arrhythmias, sudden cardiac death.
Clinical Pearls
- Cardiomyopathy is often the end stage of diverse cardiac diseases.
- Familial HCM involves sarcomeric protein mutations, autosomal dominant.
- Core heart failure therapy includes ACE inhibitors, Ξ²-blockers, diuretics, digoxin, device therapy.
References
- Seward JB, Casaclang-Verzosa G. Infiltrative cardiovascular diseases: cardiomyopathies that look alike. J Am Coll Cardiol. 2010;55(17):1769-1779.
- Elliott PM, Anastasakis A, Borger MA, et al; ESC Task Force on HCM. 2014 ESC guidelines for diagnosis and management of hypertrophic cardiomyopathy. Eur Heart J. 2014;35(39):2733-2779.
- Japp AG, Gulati A, Cook SA, et al. The diagnosis and evaluation of dilated cardiomyopathy. J Am Coll Cardiol. 2016;67(25):2996-3010.