BASICS
Description
- Neurological syndrome caused by lesion of sympathetic pathway.
- Classic triad: ipsilateral miosis, ptosis, and anhidrosis.
- Iris heterochromia seen in congenital cases (children).
- Also known as Bernard syndrome.
Epidemiology
- Pediatric incidence: 1.42 per 100,000 in patients <19 years.
- Birth prevalence for congenital cases: 1 in 6,250.
- Adult incidence unknown.
ETIOLOGY AND PATHOPHYSIOLOGY
Pathway
- Sympathetic innervation disruption to the eye and face.
- Ptosis: loss of sympathetic tone to Müller muscle causing mild eyelid droop (<2 mm).
- Miosis: impaired pupillary dilation; affected pupil smaller, especially in dim light.
- Anhidrosis: loss of facial/neck sweating; helps localize lesion level.
Causes in Adults
- Arnold-Chiari malformation, basal meningitis (e.g., syphilis)
- Cerebrovascular accident, Wallenberg syndrome
- Cervical trauma, spondylosis, demyelinating disease (MS)
- Tumors: Pancoast tumor, thyroid, mediastinum, nasopharyngeal
- Carotid artery dissection, aneurysm, central venous catheterization
- Thoracic outlet syndrome, cluster headaches
- Infectious: herpes zoster, Lyme disease
- Post-surgical: neck/chest procedures
Causes in Children
- Birth trauma, brachial plexus injury (most common)
- Neuroblastoma
- Brainstem glioma
- Vascular anomalies
- Surgical trauma
- Idiopathic
Genetics
- Rare autosomal dominant inheritance.
RISK FACTORS
- Recent head, neck, thoracic trauma
- Smoking (Pancoast tumor)
- Known vascular aneurysms
- History of neck or thoracic surgery
- Cluster headache history
DIAGNOSIS
History
- Onset (acute vs chronic)
- Visual symptoms: blurred vision, diplopia, field loss
- Pain: ipsilateral head, neck, face
- Trauma or surgery history
- Associated neurological symptoms
- Presence of sweating or flushing abnormalities
- In children: note iris color changes (heterochromia)
- Red flag: acute-onset with ipsilateral pain—consider carotid artery dissection
Physical Exam
- Measure anisocoria in bright and dim light (anisocoria more pronounced in dim light).
- Sluggish pupillary dilation (dilation lag) in affected eye.
- Mild upper eyelid ptosis (<2 mm) and possible lower lid "reverse ptosis".
- Ipsilateral conjunctival injection, nasal congestion.
- Biomicroscopic exam: iris color, structure, nystagmus.
- Full cranial nerve exam.
- Neck exam for masses, trauma.
- Neurologic and chest exam.
Differential Diagnosis
- Physiologic anisocoria (<1 mm variation)
- Third nerve palsy
- Myasthenia gravis
- Pharmacologic causes (miotics/mydriatics, various drugs)
Diagnostic Tests
- Labs: CBC, syphilis serology (FTA-ABS, VDRL), PPD, urinary VMA/HVA (pediatric neuroblastoma screen).
- Imaging:
- Chronic: MRI head/neck/chest with contrast + MRA for carotids and chest apex.
- Acute/unable to tolerate MRI: CT head/neck/chest + CTA; follow with MRI if negative.
- Consider carotid angiogram if equivocal.
- Pediatric: MRI brain, neck, chest ± abdomen if neuroblastoma suspected.
- Pregnancy: MRI considered safe; gadolinium contrast category C.
Pharmacological Testing
- Apraclonidine 0.5% drops: reverses anisocoria by dilating affected pupil due to denervation hypersensitivity (positive test = affected pupil dilates).
- Cocaine 4-10% drops: blocks norepinephrine reuptake, dilates normal pupil but not affected one (positive test = lack of dilation in affected eye).
- Hydroxyamphetamine 1% drops: differentiates lesion localization.
- Dilation of both pupils = first- or second-order neuron lesion.
- No dilation of affected pupil = third-order neuron lesion.
TREATMENT
General Measures
- Exclude life-threatening causes urgently.
- Address ptosis for cosmesis/visual impairment if persistent >12 months.
Medications
- Carotid artery dissection: thrombolysis, anticoagulation, or antiplatelet therapy.
- Mild ptosis: oxymetazoline 0.1% ophthalmic drops raise eyelid by ~1–1.3 mm; onset 2 hours, lasts ~8 hours.
- Side effects: eye discomfort, headache, dry eye.
Referral
- Neurosurgery, oncology, neurology, pulmonology, interventional radiology, oculoplastics depending on etiology.
Surgery
- Ptosis repair for cosmesis or visual impairment after 12 months (oculoplastic surgery).
ONGOING CARE
Prognosis
- Postganglionic lesions usually benign.
- Central/preganglionic lesions have worse prognosis.
Complications
- Chronic pupillary constriction
- Cosmetic concerns from ptosis and anisocoria.
REFERENCES
- Chen Y, Morgan ML, Palau AEB, et al. Evaluation and neuroimaging of the Horner syndrome. Can J Ophthalmol. 2015;50(2):107-111.
- Antonio-Santos AA, Santo RN, Eggenberger ER. Pharmacological testing of anisocoria. Expert Opin Pharmacother. 2005;6(12):2007-2013.
- Koc F, Kavuncu S, Kansu T, et al. The sensitivity and specificity of 0.5% apraclonidine in the diagnosis of oculosympathetic paresis. Br J Ophthalmol. 2005;89(11):1442-1444.
- Chen PL, Chen JT, Lu DW, et al. Comparing efficacies of 0.5% apraclonidine with 4% cocaine in the diagnosis of Horner syndrome in pediatric patients. J Ocul Pharmacol Ther. 2006;22(3):182-187.
- Sadaka A, Schockman SL, Golnik KC. Evaluation of Horner syndrome in the MRI era. J Neuroophthalmol. 2017;37(3):268-272.
- Slonim CB, Foster S, Jaros M, et al. Association of oxymetazoline hydrochloride, 0.1%, solution administration with visual field in acquired ptosis: a pooled analysis of 2 randomized clinical trials. JAMA Ophthalmol. 2020;138(11):1168-1175.
Clinical Pearls
- Triad: ipsilateral miosis, ptosis (<2 mm), anhidrosis.
- Anisocoria is more pronounced in dim light.
- Acute Horner syndrome with ipsilateral head/neck pain = carotid artery dissection until proven otherwise.
- Apraclonidine test preferred over cocaine drops for diagnosis.
- Oxymetazoline 0.1% eye drops can transiently improve mild ptosis.