Nephrotic Syndrome
BASICS
Description
- Constellation of clinical/lab findings:
- Massive proteinuria (>3.5 g/1.73 m²/24hr)
- Hypoalbuminemia (<3 g/dL)
- Severe hyperlipidemia (total cholesterol often >380 mg/dL)
- Peripheral edema
- Increased risk of thrombotic disease
- Can be due to intrinsic renal disease or secondary to infections, diabetes, SLE, neoplasia, drugs
- Associated with many kidney diseases
EPIDEMIOLOGY
- Children:
- Minimal change disease (MCD) most common (<10 yrs, 90%)
- Adults:
- Membranous nephropathy: most common primary (40%)
- Focal segmental glomerulosclerosis (FSGS): 35%; common in African Americans
- Amyloidosis: 4–17% of idiopathic cases
- Lupus nephropathy: women > men (10:1)
- Membranoproliferative GN: often in systemic viral or rheumatic illness
- Incidence:
- Adults: ~3/100,000/yr
- Children: 2–7/100,000 (<18 yrs), higher in African American/Hispanic
ETIOLOGY AND PATHOPHYSIOLOGY
- Mechanism:
- Increased glomerular permeability → protein loss (esp. albumin)
- Edema: renal salt retention + low plasma oncotic pressure
- Hypercoagulability: loss of antithrombin III in urine
- Types:
- Primary (MCD, FSGS, MGN, IgA nephropathy)
- Secondary (diabetic nephropathy, amyloidosis, paraproteinemia)
- Genetics:
- Podocyte gene mutations in familial nephrotic syndrome
RISK FACTORS
- Drug addiction (heroin—FSGS)
- Hepatitis B/C, HIV, CMV, parvovirus B19, toxoplasmosis
- Nephrotoxic drugs (NSAIDs, lithium, gold, penicillamine, bisphosphonates)
- Immunosuppression
- Cancer (esp. MGN, MCD)
- Chronic NSAID use
- Diabetes mellitus
- Preeclampsia
GENERAL PREVENTION
- Avoid causative meds (NSAIDs, gold, penicillamine, captopril)
- Avoid heroin abuse, high-risk sexual behaviors
- Tight glycemic control
DIAGNOSIS
History
- Edema, weight gain, abdominal/fluid shift, puffy eyelids, scrotal swelling, SOB
- Foamy/frothy urine, oliguria
- Joint/rash/systemic Sx (SLE), infections, fever
- Drug history, prior venous thromboembolism
Physical Exam
- Peripheral edema, ascites, pleural effusion
- Pericardial rub, decreased breath sounds (pleural effusion)
- 25% have arterial hypertension
- Macroscopic hematuria rare; microscopic hematuria in 20%
Alert: Watch for thromboembolic disease (e.g., PE), a life-threatening complication.
Differential Diagnosis
- Edema/proteinuria: see causes above
- Edema only: CHF, cirrhosis, hypothyroid, hypoalbuminemia, protein-losing enteropathy
Diagnostic Tests
- Initial:
- Urine dipstick (3+ or 4+), 24-hr urine or spot urine protein:creatinine ratio
- CBC, coagulation, renal function, glucose, albumin, lipid panel, LFTs
- ANA/dsDNA (SLE), complement (C3/C4), SPEP/UPEP (paraproteinemia)
- Hepatitis B/C, HIV, syphilis serology
- Renal US (shape, size), CXR (effusion/infection), Doppler US (DVT if suspected)
- Follow-up:
- Genetic testing (NPHS1, NPHS2) in infants/steroid-resistant children
- Other:
- Renal biopsy (adults or atypical pediatric cases)
- Contraindicated if: small kidneys, tumor/cysts, infection, severe HTN, bleeding, uncooperative
- Interpretation:
- Light microscopy: sclerosis (FSGS), diabetic nodules, mesangial hypercellularity (proliferative GN)
- IF: mesangial IgA (IgA nephropathy/HSP), other specific patterns
TREATMENT
- General:
- Monitor weight, BP, urine output, height in children
- Edema:
- Salt restriction (<2–3 g/day Na)
- Fluid restriction if hyponatremic (<1.5 L/day)
- Salt-wasting diuretics (loop/thiazide)
- Target weight loss: 0.5–1 kg/day (1–2 lb/day)
- Hyperlipidemia:
- Usually resolves with syndrome control
- Statins improve endothelial function, reduce proteinuria (except rosuvastatin—can worsen proteinuria)
- Proteinuria:
- ACE inhibitor or ARB (reduce proteinuria/progression, control HTN)
- Protein restriction (benefit unclear)
- Steroids for responsive cases (MCD, FSGS—consult nephrology)
- Second line:
- Immunosuppressives (cyclophosphamide, MMF, chlorambucil, cyclosporine) for resistant/relapsing cases
- Rituximab, abatacept (refractory cases)
- Anticoagulation (heparin/warfarin) if persistent nephrotic-range proteinuria, high risk/previous thrombosis
- Corticotropin injection (for steroid-resistant)
- Vitamin D supplement for hypocalcemia
Other
- Ambulation, range-of-motion to reduce DVT risk
- Admission criteria: respiratory distress, sepsis, thrombosis, renal failure, hypertensive crisis
ONGOING CARE
- Adjust diuretics/ACEi/ARB as per edema/proteinuria
- Monitor for relapse, progression, toxicity
- Routine immunizations: defer until remission/off immunosuppression x 3 months
Diet
- Normal protein (1 g/kg/day), low fat/cholesterol, low sodium (<2 g/day), vitamin D/iron supplements
- Fluid restriction if hyponatremic
Patient Education
PROGNOSIS
- Children (MCD): self-limited, good prognosis
- Treatable causes (infection, drug, malignancy): complete remission possible
- Aggressive forms (diabetic GN, FSGS): risk of progression to dialysis
- Relapsing/remitting course possible
COMPLICATIONS
- DVT/PE, renal/central venous thrombosis
- Pleural effusion, ascites
- Hyperlipidemia, CVD
- Acute or progressive renal failure
- Protein malnutrition/muscle wasting
ICD-10 CODES
- N04.0 Nephrotic syndrome with minor glomerular abnormality
- N04 Nephrotic syndrome (unspecified)
- N04.3 Nephrotic syndrome with diffuse mesangial proliferative GN
Clinical Pearls
- Classic tetrad: >3.5 g/day proteinuria, hypoalbuminemia, hyperlipidemia, edema
- Most pediatric cases respond to steroids and have a good prognosis
- Nondiabetic adults: always require renal biopsy to determine cause
- Maintain high suspicion for embolic events