Protein C Deficiency
BASICS
- Definition: Rare heritable or acquired prothrombotic disorder, due to deficiency of protein C (vitamin K-dependent anticoagulant).
- Symptoms: Range from asymptomatic to recurrent VTE, neonatal purpura fulminans, severe DIC.
- Protein C: Synthesized by the liver; activated protein C (APC) inhibits factors Va & VIIIa (needs protein S as cofactor).
EPIDEMIOLOGY
- Incidence: 1 in 200–500 (general), clinically substantial 1 in 20,000, severe 1 in 4 million infants
- Prevalence: 0.3% of population, 3–5% of VTE cases
- Mean age of first thrombosis: 45 years
- No gender predominance
ETIOLOGY & PATHOPHYSIOLOGY
- Heritable (autosomal dominant):
- Type I: ↓ Protein C levels (most common)
- Type II: ↓ Protein C function (normal levels)
- Acquired causes: Liver disease, DIC, severe infection, autoantibodies, cancer/chemo, vitamin K deficiency, initial warfarin use
- Genetics: >270 mutations in PROC gene; heterozygotes mild/asymptomatic; homozygotes/severe
- Risk of warfarin-induced skin necrosis (WISN): Shorter half-life of protein C compared to other vitamin K-dependent factors
RISK FACTORS
- Acquired: Heart failure, severe liver disease, DIC, vitamin K antagonists
GENERAL PREVENTION
- No preventive measures for congenital forms
- Avoid warfarin loading/bridge with heparin in known deficiency
ASSOCIATED CONDITIONS
- VTE (DVT, PE)
- Purpura fulminans in homozygotes
- Recurrent pregnancy loss
DIAGNOSIS
History
- Recurrent/unprovoked VTE (esp. <40–50 yrs)
- Thrombosis in unusual sites (mesentery, portal vein, sagittal sinus)
- Family history of VTE, abortion, or WISN
Physical Exam
- Usually normal unless active thrombosis
Differential Diagnosis
- Factor V Leiden, Protein S deficiency, antithrombin deficiency, dysfibrinogenemia, prothrombin G20210A, antiphospholipid syndrome, DIC, HIT
Testing
- Clotting/ELISA/chromogenic assay for protein C levels
- PROC gene mutational analysis
- Labs: CBC, INR, aPTT, hepatic/renal function
- Imaging as needed for VTE
When to Test
- First VTE <40 yrs
- Recurrent VTE
- VTE at unusual sites
- History of WISN
- Neonates/children with purpura fulminans
Cautions
- Acute thrombosis, warfarin, liver disease lower protein C—repeat testing after resolution
- OCPs can raise levels
TREATMENT
General
- Educate about VTE signs/symptoms
- Avoid estrogen OCPs/hormone replacement
- Progestin-only contraception is allowed
- Routine anticoagulation not recommended for asymptomatic individuals
Anticoagulation (for VTE):
- At least 3 months; longer if recurrent
- LMWH, NOACs, or warfarin (INR 2–3)
- LMWH preferred in pregnancy (monitor anti-Xa)
- Heparin bridge if starting warfarin
- Protein C concentrate for severe/homozygous cases
Pregnancy
- LMWH/UFH for VTE
- No routine prophylaxis if no prior VTE
- Postpartum prophylaxis if other risk factors
Procedures
- Hold anticoagulation for surgery
- IVC filter only if contraindication to anticoagulation
ONGOING CARE
- Monitor: INR (warfarin), anti-Xa (LMWH in pregnancy), kidney function, CBC
- Diet: Unrestricted, except if on warfarin (monitor vitamin K intake)
- Avoid NSAIDs with warfarin
PROGNOSIS
- Normal lifespan if managed appropriately
- Complications: Primary or recurrent VTE
ICD-10 CODES
- D68.59 Other primary thrombophilia
CLINICAL PEARLS
- Do not screen asymptomatic family unless female, childbearing age, no prior pregnancy complications
- Asymptomatic PCD: No prophylactic anticoagulation
- First VTE: At least 3 months anticoagulation; indefinite for recurrent VTE
- Acute thrombosis and warfarin lower protein C—repeat confirmatory testing
- Warfarin-induced skin necrosis risk: always use heparin bridge