Protein S Deficiency
BASICS
- Definition: Congenital thrombophilia (autosomal dominant), causing increased venous thromboembolism (VTE) risk.
- Protein S: Vitamin K-dependent glycoprotein, mainly liver-derived, cofactor for activated protein C (APC), inhibits Va/VIIIa (with APC), and can directly inhibit Va, VIIa, Xa.
- Only the "free" (unbound) protein S is anticoagulant; low free (but normal total) protein S = thrombosis risk.
EPIDEMIOLOGY
- Incidence: Mean first thrombosis in 2nd decade of life; affects both sexes equally
- Prevalence: ~0.2% of population; ~1% of patients with VTE
ETIOLOGY & PATHOPHYSIOLOGY
- Genetics: PROS1 gene (chromosome 3), usually heterozygous; homozygotes: neonatal purpura fulminans
- Free protein S is functional (30–40%); rest bound to C4b
- Acquired low protein S: Pregnancy, DIC, liver disease, nephrotic syndrome, HIV, acute thrombosis, varicella, OCPs, warfarin, L-asparaginase
- Risk of warfarin-induced skin necrosis: Due to shorter half-life of protein S (4–8h) vs other vitamin K factors
RISK FACTORS
- Oral contraceptives, pregnancy, HRT
- Concomitant thrombophilias
- Smoking (arterial thrombosis risk)
- Initiation of warfarin without heparin bridging
GENERAL PREVENTION
- No true primary prevention for inherited forms
- Family screening only for women considering OCPs/pregnancy with family history
ASSOCIATED CONDITIONS
- DVT, PE, superficial thrombophlebitis
- Neonatal purpura fulminans (homozygotes)
- Unusual sites: mesentery, cerebral/axillary veins
- Recurrent pregnancy losses
- Warfarin-induced skin necrosis
DIAGNOSIS
History
- Unprovoked VTE <50 yrs
- VTE with family history or known protein S deficiency
- VTE at unusual sites (mesenteric, cerebral)
- Recurrent VTE
Physical Exam
- Typically normal unless active thrombosis
Differential Diagnosis
- Other hereditary thrombophilias (Protein C, ATIII, Factor V Leiden, prothrombin G20210A, dysfibrinogenemia, etc.)
- Acquired VTE risks (immobility, cancer, surgery, pregnancy, HRT, trauma, antiphospholipid syndrome)
Testing
- Labs: CBC, PT/INR, aPTT, thrombin time, lupus anticoagulant, antiphospholipid Abs, factor V Leiden, prothrombin G20210A, antithrombin, fibrinogen, protein S antigen (total/free), protein S activity
- Timing: Avoid during acute thrombosis, pregnancy, VKA therapy, liver disease, acute illness—these lower protein S.
- Heparin does NOT affect protein S testing.
- Newborns have low protein S—use age-adjusted norms.
TREATMENT
General
- No routine anticoagulation for asymptomatic patients
- VTE treatment:
- At least 3–6 months for first VTE (longer if low/moderate bleeding risk, or recurrent VTE)
- Extended anticoagulation for 2nd unprovoked VTE or low bleeding risk
- Preferred agents:
- NOACs (rivaroxaban, apixaban, dabigatran, edoxaban) for VTE w/o cancer
- LMWH, rivaroxaban, edoxaban for VTE + active cancer
- Warfarin only after bridging with LMWH and INR 2–3 (never use alone in protein S deficiency)
- LMWH preferred over UFH (unless severe renal failure)
- Treat as outpatient if possible
- Prophylaxis: Consider in high-risk situations (surgery, immobility, postpartum, +family history)
Medications
- LMWH: enoxaparin 1 mg/kg SC BID or 1.5 mg/kg SC QD; adjust for renal function
- Fondaparinux, NOACs, warfarin (after bridging)
- Warfarin contraindicated in history of skin necrosis
- Monitor for bleeding, embolization, thrombocytopenia
ISSUES FOR REFERRAL
- Hematology for suspected cases
- Family screening: Only justified for women considering OCPs or pregnancy and with a family history
PROCEDURES/SURGERY
- Hold anticoagulation for surgery
- IVC filter: Only if anticoagulation contraindicated
ONGOING CARE
- INR monitoring for warfarin (target 2–3)
- Monitor anti-Xa if on LMWH in pregnancy/renal dysfunction
- Education: Avoid daily alcohol with warfarin, avoid NSAIDs
PROGNOSIS
- Normal lifespan
- By age 45: ~50% of heterozygotes have VTE, half are spontaneous
COMPLICATIONS
- Recurrent VTE (may require indefinite anticoagulation)
ICD-10 CODES
- D68.59 Other primary thrombophilia
CLINICAL PEARLS
- No prophylactic anticoagulation for asymptomatic protein S deficiency
- VTE in protein S deficiency: At least 6 months anticoagulation for first episode
- Always bridge with heparin when starting warfarin
- Routine family screening not indicated except select women (OCP/pregnancy with family history)